Where Science Meets Life
We are committed to researching and developing medications in cardiometabolic, pulmonary, liver, neuromuscular, and other therapeutic areas, bringing hope to those who need it most.

We Are the Leaders in RNAi
Many diseases result from excessive or abnormal protein production by specific genes. RNA interference (RNAi) is a biological mechanism cells use to regulate protein production through gene silencing.
Our proprietary TRiM™ technology enables precise and durable gene silencing across multiple tissue types.

Jill, founder of Action FCS & living with FCS, and Jon, husband & caregiver
Patient Centricity & Advocacy
Together with advocacy organizations, we’re amplifying voices, raising awareness, addressing needs of the communities we serve, and developing therapies that make a real difference in people’s lives.

Fin, father & caregiver, and Devon, living with FCS
Patient Stories
Hear from real patients living with FCS as they share their journeys of diagnosis, treatment, and hope. Discover how these individuals and families are reclaiming their lives and becoming advocates for better care.
Contact us at patientadvocacy@arrowheadpharma.com to learn more about our patient advocacy or to share your patient and caregiver story.

Expanded Access Programs
Offering access to our investigational medicines for patients with serious diseases who don’t qualify for clinical trials.

Spotlight on FCS Paper
Providing perspectives from patients and caregivers who experience living with Familial Chylomicronemia Syndrome (FCS).

Clinical Trials
Clinical trials are an essential part of our research. Discover the therapies we’re currently developing.