Father and son laughing togetherFather and son laughing together

Devon, living with FCS and Fin, father and caregiver

Science That
Changes Lives 

Where Science Meets Life 

We are committed to researching and developing medications in cardiometabolic, pulmonary, liver, neuromuscular, and other therapeutic areas, bringing hope to those who need it most.

We Are the Leaders in RNAi

Many diseases result from excessive or abnormal protein production by specific genes. RNA interference (RNAi) is a biological mechanism cells use to regulate protein production through gene silencing.

Our proprietary TRiM™ technology enables precise and durable gene silencing across multiple tissue types.

Jill, founder of Action FCS & living with FCS, and Jon, husband & caregiver

Jill, founder of Action FCS & living with FCS, and Jon, husband & caregiver

Patient Centricity & Advocacy

Together with advocacy organizations, we’re amplifying voices, raising awareness, addressing needs of the communities we serve, and developing therapies that make a real difference in people’s lives.

Fin, father & caregiver, and Devon, living with FCS

Fin, father & caregiver, and Devon, living with FCS

Patient Stories

Hear from real patients living with FCS as they share their journeys of diagnosis, treatment, and hope. Discover how
these individuals and families are reclaiming their lives 
and becoming advocates for better care.

Contact us at patientadvocacy@arrowheadpharma.com to learn more 
about our patient advocacy or to share your patient and caregiver story.

A patient speaking with a doctor

Expanded Access Programs

Offering access to our investigational medicines for patients with serious diseases who don’t qualify for clinical trials.

Man sitting on a bench staring up into the sky

Spotlight on FCS Paper

Providing perspectives from patients and caregivers who experience living with Familial Chylomicronemia Syndrome (FCS).

Doctor meeting with a patient

Clinical Trials

Clinical trials are an essential part of our research. Discover the therapies we’re currently developing.